Ultragenyx Overview
Industry: Biotechnology
Sector: Healthcare
Ultragenyx Pharmaceutical Inc., a biopharmaceutical company, focuses on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in North America, Latin America, Japan, Europe, and internationally. Its biologic products include Crysvita (burosumab), an antibody targeting fibroblast growth factor 23 for the treatment of X-linked hypophosphatemia, as well as tumor-induced osteomalacia; Mepsevii, an enzyme replacement therapy for the treatment of children and adults with Mucopolysaccharidosis VII; Dojolvi for treating long-chain fatty acid oxidation disorders; and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia. The company's products candidatures include DTX401, an adeno-associated virus 8 (AAV8) gene therapy clinical candidate for the treatment of patients with glycogen storage disease type Ia; DTX301, an AAV8 gene therapy for the treatment of patients with ornithine transcarbamylase; UX143, a human monoclonal antibody for the treatment of osteogenesis imperfecta; GTX-102, an antisense oligonucleotide for the treatment of Angelman syndrome; UX111 (ABO-102), an AAV9 gene therapy product candidate for the treatment of patients with Sanfilippo syndrome type A, or MPS IIIA, a rare lysosomal storage disease; UX701, for the treatment of Wilson disease; and UX053 for the treatment of glycogen storage disease type III. Ultragenyx Pharmaceutical Inc. has collaboration and license agreement with Kyowa Kirin Co., Ltd.; Saint Louis University; Baylor Research Institute; REGENXBIO Inc.; Bayer Healthcare LLC; GeneTx; Mereo; University of Pennsylvania; Arcturus Therapeutics Holdings Inc.; Solid Biosciences Inc.; Regeneron; Abeona; and Daiichi Sankyo Co., Ltd. The company was incorporated in 2010 and is headquartered in Novato, California. Ultragenyx Pharmaceutical Inc., a biopharmaceutical company, focuses on the identification, acquisition, development, and commercialization of novel products for the treatment of rare and ultra-rare genetic diseases in North America, Latin America, Japan, Europe, and internationally. Its biologic pr Read MoreMavefund brings filings, fundamentals, valuation, price history and news for Ultragenyx into one research view. The sections below show what strengthens or weakens the research case.
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Reported Results
What the company reported, with filing details kept small.
Quarterly result summary
Revenue was $18M (reported). Net loss was -$185. Cash was $534M.
What changed
- Revenue reported to $18M.
Guidance / outlook
No formal outlook was extracted from this filing excerpt. Open the SEC source to review full management commentary.
Source: SEC EDGAR company-filed earnings materials. Dates are shown only for verification; review the source filing before relying on extracted report details.
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Recent News
Company-relevant articles from sources that pass the Mave Signal relevance and reliability checks.
USA Rare Earth (USAR) Strengthens Its Mine-to-Magnet Strategy With Serra Verde Acquisition
Headline from Yahoo Finance: USA Rare Earth (USAR) Strengthens Its Mine-to-Magnet Strategy With Serra Verde Acquisition.
USA Rare Earth Names Serra Verde CEO as Barbara Humpton Steps Down
Headline from Yahoo Finance: USA Rare Earth Names Serra Verde CEO as Barbara Humpton Steps Down.
USA Rare Earth CEO Humpton to retire, Serra Verde's Moraitis to succeed
Headline from Reuters: USA Rare Earth CEO Humpton to retire, Serra Verde's Moraitis to succeed.
Presence: Attending An Event Is A Rare Signal, Cvent CEO Says
Headline from Forbes: Presence: Attending An Event Is A Rare Signal, Cvent CEO Says.
Canada's Enervoxa plans India rare earths project, may tie up with Vedanta, NALCO
Headline from Reuters: Canada's Enervoxa plans India rare earths project, may tie up with Vedanta, NALCO.
India and Myanmar signal closer rare earth mining ties
Headline from Reuters: India and Myanmar signal closer rare earth mining ties.
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Financial Statements
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Source: SEC EDGAR companyfacts. Values are standardized company filings for research support, not personalized financial advice.